. Intravenous 2-hydroxypropyl-β-cyclodextrin (Trappsol® Cyclo™) demonstrates biological activity and impacts cholesterol metabolism in the central nervous system and peripheral tissues in adult subjects with Niemann-Pick Disease Type C1: Results of a phase . Mol Genet Metab. 2022 Dec;137(4):309-319. Epub 2022 Oct 17 PubMed.

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This paper appears in the following:

Therapeutics

  1. Trappsol® Cyclo™